Scientist whose mother and sisters died of ALS complications hopes experimental treatment will save his life

TL;DR

Jeff Vierstra is undergoing an experimental treatment to prevent ALS, a disease that affected his family.
His mother and two sisters died from ALS, and he and his sisters share a FUS gene mutation linked to the disease.
The experimental treatment involves spinal infusions targeting the mutated gene.
After three years, Vierstra's muscle test abnormalities have normalized, and he has not developed ALS.
Researchers at Columbia University are pioneering this treatment for a rare genetic form of ALS.

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